KEGG   DRUG: Golodirsen
Entry
D11707                      Drug                                   
Name
Golodirsen (USAN/INN);
Vyondys 53 (TN)
Product
VYONDYS 53 (Sarepta Therapeutics)
Formula
C305H481N138O112P25
Exact mass
8642.9625
Mol weight
8647.2841
Remark
ATC code: M09AX08
Product: D11707<US>
Efficacy
Translation inhibitor
  Disease
Duchenne muscular dystrophy (DMD variant amenable to exon 53 skipping) [DS:H01963]
  Type
Antisense oligonucleotide
Target
DMD* [HSA_VAR:1756v1] [HSA:1756] [KO:K10366]
Brite
Anatomical Therapeutic Chemical (ATC) classification [BR:br08303]
 M MUSCULO-SKELETAL SYSTEM
  M09 OTHER DRUGS FOR DISORDERS OF THE MUSCULO-SKELETAL SYSTEM
   M09A OTHER DRUGS FOR DISORDERS OF THE MUSCULO-SKELETAL SYSTEM
    M09AX Other drugs for disorders of the musculo-skeletal system
     M09AX08 Golodirsen
      D11707  Golodirsen (USAN/INN) <US>
USP drug classification [BR:br08302]
 Genetic, Enzyme, or Protein Disorder: Replacement, Modifiers, Treatment
  Golodirsen
   D11707  Golodirsen (USAN/INN)
Target-based classification of drugs [BR:br08310]
 Not elsewhere classified
  Cellular process
   Cytoskeleton
    DMD* [HSA_VAR:1756v1]
     D11707  Golodirsen (USAN/INN) <US>
New drug approvals in the USA [br08319.html]
 New molecular entities and new therapeutic biological products
  D11707
New drug approvals in the USA, Europe and Japan [br08328.html]
 Approval dates by FDA, EMA and PMDA
  D11707
Pharmacogenomic biomarkers [br08341.html]
 Germline mutations in genetic disorder treatments
  D11707
Other DBs
CAS: 1422959-91-8
PubChem: 405226573

» Japanese version   » Back

  All links  
Ontology (6)   
   KEGG BRITE (6)   
Network (1)   
   KEGG VARIANT (1)   
Disease (1)   
   KEGG DISEASE (1)   
Chemical substance (1)   
   PubChem (1)   
Gene (2)   
   KEGG ORTHOLOGY (1)   
   KEGG GENES (1)   
All databases (11)   

Download RDF
DBGET integrated database retrieval system